OSAKA -- Kyoto University scientists have found that correcting a genetic defect that causes muscular dystrophy can alleviate the symptoms of the severest form of this debilitating disease.
Akitsu Hotta and his colleagues used induced pluripotent stem (iPS) cells -- cells reprogrammed to an embryonic state -- to test their hypothesis. While much work remains to turn their discovery into a practical treatment, it does give cause for hope.